Meta-Analysishigh evidence
Duchenne Muscular Dystrophy and Delandistrogene Moxeparvovec Gene Therapy in Children: A Systematic Review and Meta-Analysis.
Neurology. Genetics·August 1, 2026·PMID 42396397
Why it mattersThis analysis provides pooled evidence that gene therapy can improve functional outcomes and restore dystrophin in young ambulatory DMD patients, addressing a critical unmet need beyond corticosteroids and supportive care.
The papers that matter, first.
MedLit ranks the medical literature into a specialty feed with concise summaries, evidence-aware triage, and visual takeaways.
§
MedLit · Evidence, Distilled